Rapid Fire Presentation 8th International Conference on Plasmodium vivax Research 2022

Functional characterization of bone marrow and spleen-dependent P. vivax genes through CRISPR-Cas9 editing. (#112)

Alberto Ayllon-Hermida 1 2 , Marc Nicolau 1 , Marcelo AM Brito 3 4 , Oriol Llorà-Batlle 1 , Elisabet Tintó-Font 1 , Marcus VG Lacerda 3 4 , Lauro Sumoy 2 , Alfred Cortés 1 , Hernando A A del Portillo 1 2 5 , Carmen Fernandez 1 2 6
  1. ISGlobal – Institut de Salut Global de Barcelona, Barcelona, Spain
  2. Institut d’Investigació Germans Trias i Pujol, Badalona, Barcelona, Spain
  3. Instituto de Pesquisa Clínica Carlos Borborema, Fundação de Medicina Tropical Dr Heitor Vieira Dourado, Manaus, Amazonas, Brazil
  4. Instituto Leônidas & Maria Deane, Fundação Oswaldo Cruz, Manaus, Amazonas, Brazil
  5. Institució Catalana de Recerca i Estudis Avançats (ICREA), Barcelona, Spain
  6. CIBER de Enfermedades Infecciosas (CIBERINFEC), Madrid, Spain

Among the different clinical manifestations caused by P. vivax, anaemia and splenomegaly are highly prevalent. Noticeably, the bone marrow and the spleen have recently emerged as cryptic niches of natural infections and where a large parasite biomass is hidden. Our group previously demonstrated the presence of P. vivax parasites in the bone marrow of patients during acute attacks (1). Of interest, infection induced bone marrow dyserythropoiesis and altered RNA profiles related to erythropoiesis (2). Moreover, we also demonstrated that P. vivax encodes spleen-dependent genes associated with cytoadhesion and clinical protection (3). The aim of this study is to functionally characterize selected genes from the parasite upregulated in the bone marrow and from spleen-dependent genes through the implementation of the CRISPR-Cas9 technology.

Initially, we performed global transcriptional analysis of bone marrow (BM) samples of patients from Manaus (Brazil) infected with P. vivax. Computational approaches revealed a list of genes preferentially expressed in BM as compared with peripheral blood. We also used a computational approach to select a list of spleen-dependent genes. Due to the lack of a robust in vitro culture system for P. vivax, we have generated a plasmid-construct to express those genes in P. falciparum using the CRISPR-Cas9 system. Transgenic lines are being generated and confirmed through genomic integration, transcript identification and protein expression by western blot analysis. Moreover, confocal immunofluorescence microscopy is being used to determine vivax protein localization. Last, functional binding assays will be performed to unveil the function of the selected genes using spleen fibroblasts and stromal bone marrow cells.

The functional characterization of P. vivax bone marrow and spleen ligands will enable us to gain better understanding about the physiopathology of the parasite and the parasite’s tropism towards these reticulocyte-rich tissues.

  1. Baro B, Deroost K, Raiol T, Brito M, Almeida ACG, de Menezes-Neto A, et al. Plasmodium vivax gametocytes in the bone marrow of an acute malaria patient and changes in the erythroid miRNA profile. PLoS Neglected Tropical Diseases. 2017;11(4):6–13.
  2. Brito MAM, Baro B, Raiol TC, Ayllon-Hermida A, Safe IP, Deroost K, et al. Morphological and Transcriptional Changes in Human Bone Marrow During Natural Plasmodium vivax Malaria Infections. The Journal of Infectious Diseases. 2020;(Jun 18:jiaa177):1–10.
  3. Fernandez-Becerra C, Bernabeu M, Castellanos A, Correa BR, Obadia T, Ramirez M, et al. Plasmodium vivax spleen-dependent genes encode antigens associated with cytoadhesion and clinical protection. Proceedings of the National Academy of Sciences of the United States of America [Internet]. 2020 Jun 9 [cited 2021 Feb 25];117(23):13056–65. Available from: www.pnas.org/cgi/doi/10.1073/pnas.1920596117